Safety and efficacy of alternative alglucosidase alfa regimens in Pompe disease Article

Industry Collaboration International Collaboration

cited authors

  • Case, Laura E.; Bjartmar, Carl; Morgan, Claire; Casey, Robin; Charrow, Joel; Clancy, John P.; Dasouki, Majed; DeArmey, Stephanie; Nedd, Khan; Nevins, Mary; Peters, Heidi; Phillips, Dawn; Spigelman, Zachary; Tifft, Cynthia; Kishnani, Priya S.

Publication Date

  • April 1, 2015

webpage

published in

category

keywords

  • Alglucosidase alfa
  • Clinical decline
  • Dose
  • Enzyme replacement therapy
  • Infantile onset
  • Late onset
  • Pompe disease

start page

  • 321

end page

  • 332

volume

  • 25

issue

  • 4